Nusinersen - CAS 1258984-36-9

Nusinersen (nusinersen) is an antisense oligonucleotide (ASO) for the treatment of pediatric and adult spinal muscular atrophy (SMA) that alters the way the SMN2 gene is processed and increases the production of SMN proteins, which are deficient in SMA patients.

DNA/RNA Synthesis

Cell Cycle/Checkpoint, DNA Damage/DNA Repair

1258939

0.9862

-20°C

Ice Packs

Small Compound