RNA splicing modulator-4 - CAS 3067915-73-2

RNA splicing modulator-4 (Compound A) is an orally active, brain-penetrant, and selective modulator of RNA splicing. It regulates alternative splicing events to control the inclusion or exclusion of specific exons in precursor mRNA (pre-mRNA), thereby altering the coding sequence and function of mature mRNA. RNA splicing modulator-4 is promising for research in neurodegenerative diseases (such as Huntington's disease) and cancer.

DNA/RNA Synthesis

Cell Cycle/Checkpoint, DNA Damage/DNA Repair

3067840

C21H24FN5O2

397.45

OC1=C(C=C2C(=C1)N=C(C)O2)C3=CC=C(N(C)[C@@H]4[C@H](F)[C@@]5(N[C@](C4)(CCC5)[H])[H])N=N3

-20°C

Ice Packs

Small Compound