SMN-C2 - CAS 1446311-56-3

SMN-C2 is a selective regulator of SMN2 gene splicing, a risdiplam analogue, a selective RNA-binding ligand that regulates pre-mRNA splicing and acts by binding to SMN2 pre-mRNA.SMN-C2 has the potential to be used in the study of spinal muscular atrophy (SMA) .

DNA/RNA Synthesis

DNA Damage/DNA Repair, Cell Cycle/Checkpoint

1446252

0.9914

C24H27N5O2

417.5

O=C1C(C=2N=C3N(C2)C=C(C)N=C3C)=CC=4C(O1)=CC(=CC4)N5C[C@H](C)N(CC)CC5

-20°C

Ice Packs

Small Compound